BRIEF-Rocket Pharmaceuticals Updates Registration Path For RP-A501 In Danon Disease

Reuters
2022/12/22

Dec 22 (Reuters) - Rocket Pharmaceuticals Inc :

* ROCKET PHARMACEUTICALS PROVIDES UPDATE ON ANTICIPATED REGISTRATION PATH FOR RP-A501 IN DANON DISEASE FOLLOWING END-OF-PHASE 1 FDA MEETING

* ROCKET PHARMACEUTICALS - TO PURSUE A BIOMARKER-BASED COMPOSITE ENDPOINT FOR A SINGLE ARM, OPEN-LABEL PIVOTAL TRIAL WITH A NATURAL HISTORY COMPARATOR

* ROCKET PHARMACEUTICALS INC - INITIATION OF INITIAL COMPONENT OF GLOBAL STUDY ANTICIPATED IN 1H'23

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