uniQure NV has released a corporate presentation highlighting its advancements in gene therapy and providing updates on its clinical pipeline. The company reports robust progress, including upcoming data readouts for mesial temporal lobe epilepsy (MTLE) and Fabry disease within the next three to six months. uniQure’s lead candidate, AMT-130, is positioned as a potential first disease-modifying therapy for Huntington’s disease. The presentation also notes ongoing engagement with the FDA regarding the pathway to Biologics License Application (BLA) submission, and outlines the company’s strong financial position with approximately $694.2 million in cash, cash equivalents, and investment securities as of September 30, 2025. You can access the full presentation through the link below.

Disclaimer: This news brief was created by Public Technologies (PUBT) using generative artificial intelligence. While PUBT strives to provide accurate and timely information, this AI-generated content is for informational purposes only and should not be interpreted as financial, investment, or legal advice. uniQure NV published the original content used to generate this news brief on January 13, 2026, and is solely responsible for the information contained therein.