Ultragenyx Announces Positive Longer-Term Data Demonstrating Treatment With Ux111 Gene Therapy Results in Sustained, Significant Reductions in Csf-Hs and Continued Meaningful Improvements in Clinical Function Across Multiple Developmental Domains in Children With Sanfilippo Syndrome (Mps Iiia)
THOMSON REUTERS
02/03
Ultragenyx Announces Positive Longer-Term Data Demonstrating Treatment With Ux111 Gene Therapy Results in Sustained, Significant Reductions in Csf-Hs and Continued Meaningful Improvements in Clinical Function Across Multiple Developmental Domains in Children With Sanfilippo Syndrome (Mps Iiia)