Neuren Pharmaceuticals (ASX:NEU) dosed the first patient in its Koala Phase 3 clinical trial of its drug candidate NNZ-2591 for the treatment of Phelan-McDermid syndrome (PMS), a neurological disorder with no treatment options, according to a Friday filing with the Australian bourse.
The trial evaluates the safety and efficacy of NNZ-2591 in about 160 children aged three to 12 years with PMS, the filing said.
Most of the participants in the trial are expected to start dosing or start screening during February and March, the filing added.