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Orchard Therapeutics Plc
16.70
0.0000
成交量:
- -
成交額:
621.41萬
市值:
3.80億
市盈率:
-3.94
高:
16.70
開:
16.70
低:
16.70
收:
16.70
資料載入中...
總覽
公司
新聞
公告
公司資料
公司名字:
Orchard Therapeutics Plc
交易所:
NASDAQ
成立時間:
- -
員工人數:
- -
公司地址:
- -
官網:
http://www.orchard-tx.com;www.ortx.com
郵編:
- -
電話:
- -
傳真:
- -
簡介:
Orchard Therapeutics plc是2018年8月在英格蘭和威爾士註冊成立的一家私營有限責任公司。該公司是一家處於商業化階段,並全面集成的生物製藥公司,致力於通過體內基因療法來改變嚴重危及生命的罕見疾病。他們的基因治療方法旨在將患者自身或自體的HSC轉化為基因修飾的藥物產品,通過單次給藥來治療患者的疾病。他們通過利用慢病毒載體通過離體過程將缺失或缺陷基因的功能性拷貝引入患者的自體HSC中,從而獲得該結果,產生藥物產品,然後可以在床邊將其重新引入患者體內。
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