BRIEF-Neurogene Reports Positive Interim Efficacy Data From First Four Low-Dose Pediatric Participants In Ngn-401 Gene Therapy Clinical Trial For Rett Syndrome

Reuters
12 Nov 2024
BRIEF-Neurogene Reports Positive Interim Efficacy Data From First Four Low-Dose Pediatric Participants In Ngn-401 Gene Therapy Clinical Trial For Rett Syndrome

Nov 11 (Reuters) - Neurogene Inc NGNE.O:

  • NEUROGENE REPORTS POSITIVE INTERIM EFFICACY DATA FROM FIRST FOUR LOW-DOSE PEDIATRIC PARTICIPANTS IN NGN-401 GENE THERAPY CLINICAL TRIAL FOR RETT SYNDROME

  • NEUROGENE INC - ALL PARTICIPANTS SHOW 2-POINT IMPROVEMENT IN CGI-I SCALE

  • NEUROGENE INC - PARTICIPANTS SHOW 28-52% IMPROVEMENT IN RETT SYNDROME BEHAVIOR QUESTIONNAIRE

  • NEUROGENE INC - LOW-DOSE NGN-401 WELL-TOLERATED WITH FAVORABLE SAFETY PROFILE

  • NEUROGENE INC - GAINS FDA ALIGNMENT ON POTENCY ASSAY STRATEGY FOR NGN-401

  • NEUROGENE INC - TO HALT NGN-101 CLN5 BATTEN DISEASE GENE THERAPY PROGRAM

  • NEUROGENE INC: PLANS TO PROVIDE AN UPDATE OF REGISTRATIONAL TRIAL DESIGN IN H1 2025

Source text: ID:nBw8xG8Vka

Further company coverage: NGNE.O

((Reuters.Briefs@thomsonreuters.com;))

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